Special Issue: Genome Editing and Gene Therapy

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A. A. Zamyatnin, Jr.^1,2

¹Sechenov First Moscow State Medical University, Institute of Molecular Medicine, 119991 Moscow, Russia; fax: +7 (495) 622-9632; E-mail: zamyat@belozersky.msu.ru

²Lomonosov Moscow State University, Belozersky Institute of Physico-Chemical Biology, 119991 Moscow, Russia

Received April 19, 2016

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Gene therapy is one of the most rapidly developing fields of molecular medicine. Gene therapy allows simple transfer of genetic methods aimed at correcting pathological processes into clinical practice. However, a number of technical problems still exists limiting broad use of gene therapy approaches. This special issue discusses modern methods and approaches used for the development of novel, effective, and safe agents for gene therapy.

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KEY WORDS: gene therapy, genome editing, CRISPR-Cas, viral vectors

DOI: 10.1134/S0006297916070014

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